De-Risking Rare Disease Trials
Perceptive can help you minimize risks and optimize rare disease development outcomes by:
- Tackling the complexities of lengthy rare disease trials, including those involving stem cell and gene therapies
- Minimizing central-site reader discordance in therapeutic areas where imaging is critical to accurate diagnosis
- Determining optimal randomization strategies to minimize patient numbers while achieving your development goals
- Delivering high-quality imaging data from multiple modalities to support subject enrollment and determine treatment efficacy
- Optimizing delivery platform biodistribution and establishing robust PD biomarkers that can stratify and/or assess efficacy in early genetic disease and cancer studies.